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Title:
CRISPR-CAS13 SYSTEM FOR TREATING SOD1-ASSOCIATED DISEASES
Document Type and Number:
WIPO Patent Application WO/2023/025103
Kind Code:
A1
Abstract:
Provided are CRISPR-Cas13 systems and a method of treating SOD 1-associated diseases with the same.

Inventors:
YANG HUI (CN)
WANG XING (CN)
BAI MINGLIANG (CN)
Application Number:
PCT/CN2022/114021
Publication Date:
March 02, 2023
Filing Date:
August 22, 2022
Export Citation:
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Assignee:
HUIGENE THERAPEUTICS CO LTD (CN)
CENTER FOR EXCELLENCE IN BRAIN SCIENCE AND INTELLIGENCE TECH CHINESE ACADEMY OF SCIENCES (CN)
International Classes:
C12N15/86; A61P25/00; C12N9/22; C12N15/11; C12N15/113
Domestic Patent References:
WO2021050593A12021-03-18
Foreign References:
US20190330604A12019-10-31
CN112410377A2021-02-26
US20200354716A12020-11-12
US20190002889A12019-01-03
Other References:
CHEN MIN-JIE, TANG GUI-YUE; HONG XIANG-NA; HAO PEI; JIANG JING; LI XUAN: "Research Progress on CRISPR-Cas13-mediated RNA Editing System ", BIOTECHNOLOGY BULLETIN, vol. 36, no. 3, 30 November 2020 (2020-11-30), pages 1 - 8, XP093017246, DOI: 10.13560/j.cnki.biotech.bull.1985.2019-1204
COX DAVID B. T., GOOTENBERG JONATHAN S., ABUDAYYEH OMAR O., FRANKLIN BRIAN, KELLNER MAX J., JOUNG JULIA, ZHANG FENG: "Supplementary Material for RNA editing with CRISPR-Cas13", SCIENCE, 24 November 2017 (2017-11-24), pages 1 - 69, XP055969329, DOI: 10.1126/science.aaq0180
DATABASE Protein 24 July 2019 (2019-07-24), ANONYMOUS: "CRISPR-associated protein Cas13 [Leptotrichia trevisanii]", XP093039717, retrieved from Genbank Database accession no. BBM57444
Attorney, Agent or Firm:
SHANGHAI PATENT & TRADEMARK LAW OFFICE, LLC (CN)
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