Title:
CRISPR-CAS13 SYSTEM FOR TREATING SOD1-ASSOCIATED DISEASES
Document Type and Number:
WIPO Patent Application WO/2023/025103
Kind Code:
A1
Abstract:
Provided are CRISPR-Cas13 systems and a method of treating SOD 1-associated diseases with the same.
Inventors:
YANG HUI (CN)
WANG XING (CN)
BAI MINGLIANG (CN)
WANG XING (CN)
BAI MINGLIANG (CN)
Application Number:
PCT/CN2022/114021
Publication Date:
March 02, 2023
Filing Date:
August 22, 2022
Export Citation:
Assignee:
HUIGENE THERAPEUTICS CO LTD (CN)
CENTER FOR EXCELLENCE IN BRAIN SCIENCE AND INTELLIGENCE TECH CHINESE ACADEMY OF SCIENCES (CN)
CENTER FOR EXCELLENCE IN BRAIN SCIENCE AND INTELLIGENCE TECH CHINESE ACADEMY OF SCIENCES (CN)
International Classes:
C12N15/86; A61P25/00; C12N9/22; C12N15/11; C12N15/113
Domestic Patent References:
WO2021050593A1 | 2021-03-18 |
Foreign References:
US20190330604A1 | 2019-10-31 | |||
CN112410377A | 2021-02-26 | |||
US20200354716A1 | 2020-11-12 | |||
US20190002889A1 | 2019-01-03 |
Other References:
CHEN MIN-JIE, TANG GUI-YUE; HONG XIANG-NA; HAO PEI; JIANG JING; LI XUAN: "Research Progress on CRISPR-Cas13-mediated RNA Editing System ", BIOTECHNOLOGY BULLETIN, vol. 36, no. 3, 30 November 2020 (2020-11-30), pages 1 - 8, XP093017246, DOI: 10.13560/j.cnki.biotech.bull.1985.2019-1204
COX DAVID B. T., GOOTENBERG JONATHAN S., ABUDAYYEH OMAR O., FRANKLIN BRIAN, KELLNER MAX J., JOUNG JULIA, ZHANG FENG: "Supplementary Material for RNA editing with CRISPR-Cas13", SCIENCE, 24 November 2017 (2017-11-24), pages 1 - 69, XP055969329, DOI: 10.1126/science.aaq0180
DATABASE Protein 24 July 2019 (2019-07-24), ANONYMOUS: "CRISPR-associated protein Cas13 [Leptotrichia trevisanii]", XP093039717, retrieved from Genbank Database accession no. BBM57444
COX DAVID B. T., GOOTENBERG JONATHAN S., ABUDAYYEH OMAR O., FRANKLIN BRIAN, KELLNER MAX J., JOUNG JULIA, ZHANG FENG: "Supplementary Material for RNA editing with CRISPR-Cas13", SCIENCE, 24 November 2017 (2017-11-24), pages 1 - 69, XP055969329, DOI: 10.1126/science.aaq0180
DATABASE Protein 24 July 2019 (2019-07-24), ANONYMOUS: "CRISPR-associated protein Cas13 [Leptotrichia trevisanii]", XP093039717, retrieved from Genbank Database accession no. BBM57444
Attorney, Agent or Firm:
SHANGHAI PATENT & TRADEMARK LAW OFFICE, LLC (CN)
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