Title:
アンチセンス核酸
Document Type and Number:
Japanese Patent JP6647430
Kind Code:
B2
Abstract:
The present invention provides a pharmaceutical composition which causes skipping of the 53rd exon in the human dystrophin gene with a high efficiency.The present invention provides an oligomer which efficiently enables to cause skipping of the 53rd exon in the human dystrophin gene.
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Inventors:
Naoki Watanabe
Yohei Sato
Shinichi Takeda
Tetsuya Nagata
Yohei Sato
Shinichi Takeda
Tetsuya Nagata
Application Number:
JP2019001091A
Publication Date:
February 14, 2020
Filing Date:
January 08, 2019
Export Citation:
Assignee:
NIPPON SHINYAKU CO.,LTD.
National Research and Development Agency National Center for Neurology and Psychiatry
National Research and Development Agency National Center for Neurology and Psychiatry
International Classes:
C12N15/113; A61K31/712; A61K48/00; A61P21/00
Foreign References:
| WO2010048586A1 | ||||
| US20100168212 |
Attorney, Agent or Firm:
Hiroshi Kobayashi
Norio Omori
Emiko Nishizawa
Tomohiro Maruyama
Yasuhito Suzuki
Norio Omori
Emiko Nishizawa
Tomohiro Maruyama
Yasuhito Suzuki